News & Events

Boston, December 6, 2025Vertex Pharmaceuticals announced new clinical data demonstrating that its gene-editing therapy Casgevy (exagamglogene autotemcel, exa-cel) produced robust therapeutic benefits ...

December 3, 2025 — Capricor Therapeutics announced that its investigational cell therapy Deramiocel achieved both primary and key secondary endpoints in the pivotal Phase 3 HOPE-3 trial for Duchenne ...

December 1, 2025 — Regeneron Pharmaceuticals announced today a global collaboration with Tessera Therapeutics to develop and commercialize Tessera’s investigational in-vivo gene editing therapy TSRA...

South San Francisco, CA — November 3, 2025 — Biotech leader Genentech announced that it will present 46 abstracts, including 12 oral presentations, from its hematology portfolio at the upcoming ASH ...

A newly released market report on November 26, 2025 indicates that the global oncolytic virus CDMO services market is entering a phase of accelerated growth. According to the report, the market is pro...

Washington, Nov 24, 2025 — The U.S. Food and Drug Administration (FDA) has approved Itvisma, a gene therapy developed by Novartis, for a broader group of patients with spinal muscular atrophy (SMA), ...

November 2025 — As the cell and gene therapy (CGT) landscape continues to expand, the need for robust aseptic monitoring and contamination control is growing rapidly. According to a recent industry r...

Frankfurt, Germany · November 2025 — On November 6, 2025, the Cellex Symposium 2025 was successfully held in Frankfurt, Germany, bringing together over 100 leading scientists, industry executives, r...

The U.S. Food and Drug Administration (FDA) has added a boxed warning—its most serious level of safety alert—to Sarepta Therapeutics’ gene therapy Elevidys, following the deaths of two Duchenne mus...

November 2025 · Silver Spring, Maryland — The U.S. Food and Drug Administration (FDA) has announced a new “Plausible Mechanism” approval pathway to accelerate the review and authorization of ultra...

October 2025 · Cambridge, Massachusetts — Kelonia Therapeutics announced today a strategic collaboration with Johnson & Johnson to advance the development of in vivo CAR-T cell therapies, a next...

October 2025 · London, UK — A new study led by researchers at University College London (UCL) and Great Ormond Street Hospital has confirmed the long-term safety and efficacy of gene therapy for tre...